| Wissenschaftl. Titel | Two part (double-blind inclisiran versus placebo [Year 1] followed by open-label inclisiran [Year 2]) randomized multicenter study to evaluate safety, tolerability and efficacy of inclisiran in children (2 to less than 12 years) with homozygous familial hypercholesterolemia and elevated LDL-cholesterol (ORION-19) |
| Erkrankung |
Drüsen/Hormone/Stoffwechsel:
Hypercholesterinämie/LDL
|
| weitere Prüfzentren | |
| Kurzprotokoll | Kurzprotokoll |
| Links | Zu den Ein- und Ausschlusskriterien |
erstellt 13.01.2026 Admin02
geändert 13.01.2026 Admin02